6m
16 Nov 2023

UK approves groundbreaking gene therapy treatment for sickle cell

Health and Social Care Editor

The UK’s medicines watchdog has approved a groundbreaking gene therapy treatment for sickle cell disease – which could transform the lives of thousands of people with the debilitating blood disorder.

The treatment – called Casgevy – works by editing faulty genes to help the body produce functioning haemoglobin –  and experts have called it “an historic moment for the sickle cell community”.